BioMarin focuses on developing treatments for rare diseases. It’s expected to report third quarter results this week.
Goldman says that the company has room for growth with its recently launched Palynziq, which treats adult phenylketonuria, a rare inherited disorder in which the body can’t process an amino acid called phenylalanine
Goldman also said treatments with potential include vosoritide (treats achondroplasia, a type of short-limbed dwarfism), val-rox (hemophilia A gene therapy), and BMN250 (treats Sanfilippo Syndrome B).
Source: Business Insider
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